Professor Datuk Dr. Abdul Rahman Abdul Jamal
Senior Consultant in Pediatric Hematology-Oncology and Molecular Genetics,
Universiti Kebangsaan Malaysia (UKM),
Senior Principal Research Fellow, UKM Medicine Molecular Biology Institute,
Kuala Lumpur, Malaysia
In a world-first, researchers designed, tested, and delivered a personalized CRISPR therapy to an infant with a fatal urea cycle disorder.1 The treatment specifically targeted a rare mutation in the carbamoyl phosphate synthetase 1 (CPS1)
August 22, 2025
